Dedicated to finding a cure for APBD,

while improving the lives of those affected

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Moving the needle for APBD research

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    We invite you to join our APBD Tour de Friends Rally for Research campaign to raise $150,000 for life-saving APBD research.

    Now through May 16, every donation made will be matched, dollar-for-dollar, up to $50,000, thanks to our Board of Directors. Your support funds vital APBD research, bringing us closer to treatments and improving lives.

    We’re partnering with Alex The Leukodystrophy Charity and Association for Glycogen Storage Disease-UK for a special event designed to bring our global community together to connect, share experiences, and find support.

    Welcome Remarks — 2022 APBD Scientific & Community Conference
    10:59

    Orhan Akman, PhD discusses antisense oligonucleotide (ASO) as a novel therapeutic approach for APBD
    22:43

    APBD PSA 7 13
    1:36

    We Are APBD
    6:17

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